福克斯新闻 美国药管局批准第一种针对遗传病的基因疗法

Advisors¹ to the Food and Drug Administration are meeting Thursday to consider giving the go ahead to gene² therapy aimed at improving vision for some people with hereditary³ blindness.

It would be the first gene therapy in the U.S. for an inherited disease and the first in which a corrective gene is given directly to a patient. The eye treatment Luxturna is intended to be given just once and supplies a gene to make a protein needed for sight which is missing in people with a defective⁴ gene. A study of 29 patients found it improved vision for nearly all who received it and it seemed safe.

Luxturna is made by Philadelphia based Spark Therapeutics.

Lilian Woo, FOX News.

周四，美国食品和药物管理局的顾问召开会议，商讨批准用于恢复遗传失明患者视力的基因治疗方案。

该方案为美国首个针对遗传病的基因治疗方案，同时也是首个直接向患者注射基因正常拷贝的治疗方案。该方案名为“Luxturna基因疗法”，只需注射一次，就能给有基因缺陷的患者提供转换蛋白质所需的基因。有研究表明，受试的29名患者的视力几乎都有了改善，该方案似安全可靠。

研发该疗法的是费城的火花基因疗法公司。

福克斯新闻，我是Lilian Woo。

1 advisors   

n.顾问，劝告者( advisor的名词复数 )；（指导大学新生学科问题等的）指导教授

参考例句：

• The governors felt that they were being strung along by their advisors. 地方长官感到他们一直在受顾问们的愚弄。 来自《现代汉英综合大词典》
• We will consult together with advisors about her education. 我们将一起和专家商议她的教育事宜。 来自互联网

2 gene   

n.遗传因子，基因

参考例句：

• A single gene may have many effects.单一基因可能具有很多种效应。
• The targeting of gene therapy has been paid close attention.其中基因治疗的靶向性是值得密切关注的问题之一。

3 hereditary   

adj.遗传的，遗传性的，可继承的，世袭的

参考例句：

• The Queen of England is a hereditary ruler.英国女王是世袭的统治者。
• In men,hair loss is hereditary.男性脱发属于遗传。

4 defective   

adj.有毛病的，有问题的，有瑕疵的

参考例句：

• The firm had received bad publicity over a defective product. 该公司因为一件次品而受到媒体攻击。
• If the goods prove defective, the customer has the right to compensation. 如果货品证明有缺陷， 顾客有权索赔。